Edited stem cells offer hope of precision therapy for blindness – Medical Xpress
Medical Xpress |
Edited stem cells offer hope of precision therapy for blindness
Medical Xpress Skin cells from a patient with X-linked Retinitis Pigmentosa were transformed into induced pluripotent stem cells and the blindness-causing point mutation in the RPGR gene was corrected using CRISPR/Cas9. Credit: Vinit Mahajan, University of Iowa … Precision Medicine: Genetic Repair of Retinitis Pigmentosa in Patient-Derived Stem Cells CRISPR used to repair blindness-causing genetic defect in patient-derived stem cells |
