Stem cell-transplantation therapy for adrenoleukodystrophy: current perspectives – Dove Medical Press
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Stem cell-transplantation therapy for adrenoleukodystrophy: current perspectives
Dove Medical Press Abstract: Adrenoleukodystrophy (ALD) is a rare, X-linked peroxisomal disorder of impaired very long-chain fatty-acid metabolism. It results from various mutations in the ABCD1 gene (Xq28). All males with the biochemical defect of ALD are at risk of … |
