Gene Therapy Treats Sickle Cell Disease in Teenager Using Lentiviral Vector – Medscape
Medscape |
Gene Therapy Treats Sickle Cell Disease in Teenager Using Lentiviral Vector
Medscape Gene therapy that delivered an antisickling variant of hemoglobin in an autologous hematopoietic stem cell (HSC) transplant has ameliorated symptoms of severe sickle cell disease (SCD) in a 15-year-old boy, according to a report published in the March … Gene therapy lets a French teen dodge sickle cell disease Gene Therapy: A Breakthrough for Sickle Cell Anemia? One boy's cure raises hopes and questions about gene therapy for sickle cell disease |
