Pioneering stem cell gene therapy cures infants with bubble baby disease – Medical Xpress
Medical Xpress |
Pioneering stem cell gene therapy cures infants with bubble baby disease
Medical Xpress UCLA researchers have developed a stem cell gene therapy cure for babies born with adenosine deaminase-deficient severe combined immunodeficiency, a rare and life-threatening condition that can be fatal within the first year of life if left untreated. |
