ADA-SCID (aka Bubble Baby Disease) Cured by Gene Therapy – Rare Disease Report
Rare Disease Report |
ADA-SCID (aka Bubble Baby Disease) Cured by Gene Therapy
Rare Disease Report A study published in in the Journal of Clinical Investigation revealed that gene therapy cured 9 of 10 children with adenosine deaminase-deficient severe combined immunodeficiency (ADA-SCID, aka Bubble Boy Disease). Children in the ground-breaking … |
