Bubble boy hope: Strimvelis gene therapy revises genetic make-up, offers rare immune deficiency cure – Genetic Literacy Project
Genetic Literacy Project |
Bubble boy hope: Strimvelis gene therapy revises genetic make-up, offers rare immune deficiency cure
Genetic Literacy Project Gene therapies are more complex than ordinary pills, and the diseases they treat affect few people. But sky-high prices have raised questions about whether patients can access them. Strimvelis, used to treat an ultra-rare immune deficiency, has a list … |
