Gene Therapy for Rare Blistering Skin Disorder Gets FDA Orphan Designation – Rare Disease Report
Rare Disease Report |
Gene Therapy for Rare Blistering Skin Disorder Gets FDA Orphan Designation
Rare Disease Report On Thursday, the company announced their 3rd gene therapy received an FDA orphan designation; this one for the treatment of epidermolysis bullosa (EB). The other 2 gene therapies that the company has orphan drug designations are for the treatments of … |
