News from the AAN Annual Meeting: Gene Therapy Found to Benefit Infants with SMA Type 1 in Open-Label Trial – LWW Journals
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News from the AAN Annual Meeting: Gene Therapy Found to Benefit Infants with SMA Type 1 in Open-Label Trial
LWW Journals In a new gene therapy trial, infants with spinal muscular atrophy survived longer without adverse events and achieved developmental milestones. Independent experts said the therapy should be studied and compared with the recently-approved drug, … |
