Philly biotech’s first-ever gene therapy progresses with FDA – Philly.com
Philly.com |
Philly biotech's first-ever gene therapy progresses with FDA
Philly.com If approved, the treatment would be the first gene therapy for a genetic disease in the United States. Spark's treatment, called voretigene neparvovec, streams genes directly into the eye's retina. It has been granted priority review by the FDA because … FDA embraces the first US application for a gene therapy, offering an accelerated test case Spark files revolutionary gene therapy with FDA FDA accepts biologics license application for voretigene neparvovec |
