Gene Therapy for OPMD Nears Human Studies, Benitec Announces – Muscular Dystrophy News
Muscular Dystrophy News |
Gene Therapy for OPMD Nears Human Studies, Benitec Announces
Muscular Dystrophy News A single gene therapy that silences the mutation responsible for oculopharyngeal muscular dystrophy (OPMD) and replaces the mutated gene with a normal one may advance into human studies in the second half of 2018. Benitec Biopharma started its OPMD … |
