Part 3 of Gene Therapy Trial for MPS IIIA (Sanfilippo A) Has Begun – Rare Disease Report
Rare Disease Report |
Part 3 of Gene Therapy Trial for MPS IIIA (Sanfilippo A) Has Begun
Rare Disease Report On Monday, Rare Disease Report covered the release of new information from Abeona Therapeutics' gene therapy trial for patients with mucopolysaccharidosis type IIIA (MPS IIIA, Sanfilippo syndrome). One year data from Cohort 1 in the company's 3-cohort, … |
