As Blindness Gene Therapy Nears FDA Finish Line, A Shout-Out to Activist Families – PLoS Blogs (blog)
PLoS Blogs (blog) |
As Blindness Gene Therapy Nears FDA Finish Line, A Shout-Out to Activist Families
PLoS Blogs (blog) Today I'm glued to my laptop, watching and listening to physicians, researchers, family members, and patients present their cases for FDA approval of Luxturna (voretigene neparvovec), the gene therapy that Corey, now a high school senior, received. He … |
