Gene Therapy for HD Continues to Show Promise – Rare Disease Report (blog)
Rare Disease Report (blog) |
Gene Therapy for HD Continues to Show Promise
Rare Disease Report (blog) At the European Society of Gene and Cell Therapy (ESGCT) Congress in Berlin, Germany today, uniQure – the company that developed the first ever approved gene therapy (for familial chylomicronemia syndrome) – presented new preclinical data showing … |
