Gene Therapy Approach Using HAC Vector May Work with Dystrophin Gene, Study Suggests – Muscular Dystrophy News
Muscular Dystrophy News |
Gene Therapy Approach Using HAC Vector May Work with Dystrophin Gene, Study Suggests
Muscular Dystrophy News Gene therapy aims to treat DMD, caused by mutations in the dystrophin gene, by delivering the correct version of the gene to patients' cells to replace the faulty version. But the considerable size of the dystrophin gene makes it difficult for … |
