Researchers Discover Promising New Gene Therapy Approach for Spinal Muscular Atrophy – SMA News Today
SMA News Today |
Researchers Discover Promising New Gene Therapy Approach for Spinal Muscular Atrophy
SMA News Today The iPSCs were then genetically modified to convert the SMN2 gene into a SMN1-like gene using the CRISPR/Cpf1 gene editing system. This system, similar to CRISPR-Cas9, allows researchers to edit parts of the genome by adding, removing, or changing … |
