Gene Therapy May Be Cure for Some With Rare Blood Disorder – Philly.com
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Gene Therapy May Be Cure for Some With Rare Blood Disorder
Philly.com Beta-thalassemia can be cured through a bone marrow transplant from a brother or sister, but that's not an option for most, Thompson said. "Unfortunately, the majority of individuals with thalassemia will not have a suitable matched sibling," Thompson … |
