Gene therapy offers potential cure for patients with lipoprotein lipase deficiency – News-Medical.net
News-Medical.net |
Gene therapy offers potential cure for patients with lipoprotein lipase deficiency
News-Medical.net During the first 18 months after treatment with ali-pogene tiparvovec, a gene therapy recently approved in Europe to treat lipoprotein lipase deficiency (LPLD), the first patient to receive the treatment had no abdominal pain or episodes of … |
