Gene Therapy for ALD – GenomeWeb
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Gene Therapy for ALD
GenomeWeb Researchers have used gene therapy to treat boys with adrenoleukodystrophy, the New York Times reports. Boston Children’s Hospital’s David Williams and his colleagues conducted a small study involving 17 boys with the disease. ALD is caused by a … |
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bluebird bio unveils positive, albeit early, data for gene therapy
BioPharma Dive Published in the New England Journal of Medicine, the study results showed bluebird bio’s hematopoietic stem-cell gene therapy met the primary endpoint, with 15 of the 17 patients (or 88%) receiving the therapy free of major functional disabilities … |
Pharmaceutical Processing |
Abeona’s gene therapy ABO-102 shows durable treatment effect in Sanfilippo study
Seeking Alpha One-year data from Cohort 1 in Abeona Therapeutics’ (ABEO -1.9%) Phase 1/2 clinical trial assessing a single IV injection of gene therapy ABO-102 in patients with Sanfilippo syndrome Type A (MPS IIIA) showed a significant and durable treatment effect. Commercial Gene Therapy Manufacturing Facility Slated For …Pharmaceutical Processing Abeona Announces Top-Line One Year Data from ABO-102 MPS IIIA Trial at ARM’s Cell & Gene Meeting on the MesaMarkets Insider Contrasting Abeona Therapeutics (ABEO) & Arena Pharmaceuticals (ARNA)Dispatch Tribunal Zacks Investment Research all 48 news articles » |
Retraction Watch (blog) |
Case report of stem cell therapy in child didn’t meet “ethical standards,” says journal
Retraction Watch (blog) A journal has retracted a recent case report about a stem cell therapy in a child with cerebral palsy, after discovering the study failed to meet “ethical standards.” According to the journal, Regenerative Medicine, the ethical issue is that the … Stem cell gene therapy safe for adrenoleukodystrophyMedical Xpress Hematopoietic stem–cell gene therapy for cerebral adrenoleukodystrophyPharmacy Today, American Pharmacists Association, pharmacist.com |
Retraction Watch (blog) |
Case report of stem cell therapy in child didn’t meet “ethical standards,” says journal
Retraction Watch (blog) A journal has retracted a recent case report about a stem cell therapy in a child with cerebral palsy, after discovering the study failed to meet “ethical standards.” According to the journal, Regenerative Medicine, the ethical issue is that the … Stem cell gene therapy safe for adrenoleukodystrophyMedical Xpress Hematopoietic stem–cell gene therapy for cerebral adrenoleukodystrophyPharmacy Today, American Pharmacists Association, pharmacist.com |
Retraction Watch (blog) |
Case report of stem cell therapy in child didn’t meet “ethical standards,” says journal
Retraction Watch (blog) A journal has retracted a recent case report about a stem cell therapy in a child with cerebral palsy, after discovering the study failed to meet “ethical standards.” According to the journal, Regenerative Medicine, the ethical issue is that the … |
Futurism |
CRISPR Is on the Cusp of Eradicating a Host of Diseases
Futurism The CRISPR/Cas9 gene editing tool has had a busy year. It recently removed genetic disorders from human embryos, targeted the “command center” of cancer, extracted HIV from a living organism, and forced superbugs to kill themselves. This is all … Crispr Theraptc (CRSP) Earns Daily News Impact Rating of 0.11The Ledger Gazette |
Key Gazette |
Barclays Starts Coverage on Editas Medicine, Inc. (EDIT) With A Rating Of “Overweight”
First News 24 CRISPR uses a protein-ribonucleic acid (RNA) complex composed of an enzyme, including either Cas9 (CRISPR associated protein 9) or Cpf1 (CRISPR from Prevotella and Francisella 1), bound to a guide RNA molecule designed to recognize a particular … Editas Medicine, Inc. (NASDAQ:EDIT) Closed 6.5% Above Its 50 …HugoPress |