‘Butterfly boy’ Jonathan Pitre cleared for second stem cell transplant – Ottawa Sun
Ottawa Sun |
‘Butterfly boy’ Jonathan Pitre cleared for second stem cell transplant
Ottawa Sun Last September, Pitre suffered nausea, hair loss, fevers and exhaustion in the aftermath of his first transplant, which ultimately failed when his own stem cells recolonized his bone marrow. His second transplant has been delayed because of lung and … |
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Stem cell transplant offers first-ever cure for rare blood disorder
Becker’s Hospital Review A new stem cell transplant technique that does not require the use of high-dose chemotherapy and radiation successfully cured an adult patient with congenital dyserythropoietic anemia, marking the first documented cure of the condition, according to a … Medical breakthrough: first patient cured of a rare and painful blood disorder called CDAZME Science Avoiding High-Dose Chemotherapy and Radiation Successfully Treated CDA Patient [VIDEO]Counsel & Heal |
Ottawa Citizen |
‘Butterfly boy’ Jonathan Pitre cleared for second stem cell transplant
Ottawa Citizen Fully recovered from a series of infections, Jonathan Pitre has received medical clearance to undergo a second stem cell transplant. Pitre, 16, will check into hospital on the last day of March to begin eight days of high-dose chemotherapy and one day … |
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Neurocrine fleshes out its PhIII case for valbenazine; Avrobio adds to gene therapy pipeline
Endpoints News The PDUFA date for the breakthrough therapy is April 11. → Cambridge, MA-based biotech Avrobio is expanding its gene therapy pipeline. Investigators are adding a preclinical program for Gaucher disease, which will follow their Phase I for Fabry disease. |
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CRISPR finds drug synergy
Nature.com Certain combinations of drugs might kill drug-resistant tumours, and a method based on the CRISPR–Cas9 gene-editing system offers a way to find them. Tumours often become resistant to individual drugs, leading clinicians to use combinations of … |