Exton biotech testing gene therapy for devastating skin disorder – 6abc.com
6abc.com |
Exton biotech testing gene therapy for devastating skin disorder
6abc.com A Chester County biotech firm now has the FDA’s OK to begin pediatric tests on its breakthrough drug. It could ease suffering for thousands with a devastating skin disorder known as RDEB. “As soon as he was born, they knew something was wrong … |
OncLive |
Immunotherapy Options in Refractory CRC
OncLive Transcript: John L. Marshall, MD: All right, let’s shift gears back to the sense of hope that’s out there and the new therapies that are emerging in refractory and other lines of therapy. Everybody’s favorite topic is, of course, immunotherapy. Johanna … |
OncLive |
Immunotherapy Options in Refractory CRC
OncLive Transcript: John L. Marshall, MD: All right, let’s shift gears back to the sense of hope that’s out there and the new therapies that are emerging in refractory and other lines of therapy. Everybody’s favorite topic is, of course, immunotherapy. Johanna … |
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Gene Therapy May Be Cure for Some With Rare Blood Disorder
Philly.com Beta-thalassemia can be cured through a bone marrow transplant from a brother or sister, but that’s not an option for most, Thompson said. “Unfortunately, the majority of individuals with thalassemia will not have a suitable matched sibling,” Thompson … |