Second Gene Therapy from MeiraGTx Granted Rare Pediatric Disease Designation – Rare Disease Report
Rare Disease Report |
Second Gene Therapy from MeiraGTx Granted Rare Pediatric Disease Designation
Rare Disease Report This morning, the Offices of Orphan Products Development and Pediatric Therapeutics of the U.S. Food and Drug Administration (FDA) have granted rare pediatric disease designation to MeiraGTx’s A002 (ZZV2/8-hCARp.hCNGB3). The gene therapy product … MeiraGTx Receives Rare Pediatric Disease Designation for A002 for the Treatment of Achromatopsia Due to Mutations …PR Newswire (press release) |
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Global Cancer Stem Cell Therapies Market, 2017-2030: Identification of 150+ Molecules being Investigated as …
Business Wire (press release) The Cancer Stem Cell Therapies Market, 2017-2030′ report examines the current landscape and the future outlook of the growing pipeline of products targeting CSCs. We identified over 150 molecules that are currently being investigated as therapeutic … |
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Animated map illustrates ‘wildfire spread’ of unregulated stem cell clinics in US
HealthNewsReview.org Mary Chris Jaklevic has freelanced for HealthNewsReview.org since 2016 and recently joined the staff as a full-time health care journalist. She tweets as @mcjaklevic. A newly published animated map shows how an unregulated industry of stem cell clinics … |
PLoS Blogs (blog) |
CRISPR Gene Editing of Neurons in Prader-Willi Syndrome
PLoS Blogs (blog) Since being fortunate enough a few years ago to find myself one of only two journalists in the press room at a genetics conference with two of CRISPR/Cas9’s inventors, I’ve made an effort to highlight exciting, beneficial uses of gene editing … |
SpaceCoast Living |
Stem Cell Research and Treatment
SpaceCoast Living This is an interesting circumstance. We’ll often interview a doctor for SpaceCoast Living HEALTH and then work to keep the content relative and quick to read. I originally had thought that my interview with Dr. Jasen Kobobel would be to discuss his … |