FDA approves Spark’s gene therapy for rare blindness pioneered at CHOP – Philly.com
|
FDA approves Spark’s gene therapy for rare blindness pioneered at CHOP
Philly.com The treatment, developed by Philadelphia drug maker Spark Therapeutics and researchers at Children’s Hospital of Philadelphia, and represents the first gene therapy for a genetic disease in the United States. “Today’s approval marks another first in … |
|
FDA Approves Gene Therapy for Rare Vision Loss Disease
Specialty Pharmacy Times “Today’s approval marks another first in the field of gene therapy—both in how the therapy works and in expanding the use of gene therapy beyond the treatment of cancer to the treatment of vision loss—and this milestone reinforces the potential of … |
Business Insider |
The FDA just approved the first gene therapy to treat blindness
Business Insider The US Food and Drug Administration just approved a cutting-edge gene therapy. The treatment, called Luxturna and made by Spark Therapeutics, treats Leber congenital amaurosis, a hereditary form of blindness. It’s been tested in people with the … |