Bellicum Announces Data Presentation Demonstrating Improved Immune Recovery Following Haploidentical Stem …GlobeNewswire (press release)ATLANTA, Dec. 09, 2017 (GLOBE NEWSWIRE) — Bellicum Pharmaceuticals, Inc. (NASDAQ:BLCM), a leader in developing no… Continue reading
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ASH17: BioMarin’s gene therapy promises one-time treatment of hemophilia
BioPharma Dive An experimental gene therapy from BioMarin Pharmaceuticals Inc. dramatically reduced bleeding episodes in patients with hemophilia A, boosting levels of the blood clotting protein Factor VIII to near-normal or normal levels in 11 out of 13 patients … |
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New Gene Therapy May Be Cure for ‘Bubble Boy’ Disease
U.S. News & World Report SATURDAY, Dec. 9, 2017 (HealthDay News) — Babies born with the immune-system ravaging “bubble boy” disease have had to spend their too-often-short lives in germ-free isolation, lest something as simple as a common cold virus fell them with a fatal … |
EurekAlert (press release) |
St. Jude gene therapy improves immunity in babies with ‘bubble boy’ disease
EurekAlert (press release) Early evidence suggests that gene therapy developed at St. Jude Children’s Research Hospital will lead to broad protection for infants with the devastating immune disorder X-linked severe combined immunodeficiency disorder. Preliminary results from the … |
EurekAlert (press release) |
St. Jude gene therapy improves immunity in babies with ‘bubble boy’ disease
EurekAlert (press release) Early evidence suggests that gene therapy developed at St. Jude Children’s Research Hospital will lead to broad protection for infants with the devastating immune disorder X-linked severe combined immunodeficiency disorder. Preliminary results from the … |