Gene therapy saves boy’s life – The Hindu
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Gene therapy saves boy’s life
The Hindu A boy who nearly died when disease stripped most of the skin from his body, is playing soccer two years after he received a new, gene-edited cover in an experimental procedure, the doctors who treated him have said. The boy, then seven years old, was … |
Xconomy |
Juno Dissects ROCKET Deaths, Will Aim Better CAR–T at Leukemia
Xconomy CAR-T therapy has shown great promise, knocking out otherwise untreatable cancer, at least temporarily, in dozens of adults and kids with certain types of leukemia and lymphoma. The most promising form of CAR-T uses a patient’s own T cells, drawn from … |
MD Magazine |
Gene Therapy Recovers LCA Patient Vision
MD Magazine The tested gene therapy, voretigene neparvovec (Luxturna) from Spark Therapeutics, is currently under FDA review for potential approval by January 2018. An injection therapy, it uses a genetically-modified version of a harmless virus that’s been … |