Orchard’s gene therapy gains UK ‘promising innovative medicine’ status – pharmaphorum
pharmaphorum |
Orchard’s gene therapy gains UK ‘promising innovative medicine’ status
pharmaphorum A UK biotech start-up has gained a sought after ‘promising innovative medicine’ (PIM) designation for its ultra-rare disease gene therapy. Orchard Therapeutics was only set up two years ago, but has now gained the PIM status from the UK’s medicines … |
MIT Technology Review |
Sickle-Cell Patients See Hope in CRISPR
MIT Technology Review The idea is that CRISPR could correct the genetic mutation responsible for sickle-cell so that patients’ bodies could make normal red blood cells, alleviating the pain and other severe symptoms associated with the disease. Researchers have already … |
Scope (blog) |
Current “humanized” mice not good models for studying stem cell transplants, say researchers
Scope (blog) These “humanized” mice have been useful models in some situations, such as the study of the human immune response to HIV infection or the transplantation of certain types of tissue. But recent research by cardiologist and stem cell expert Joseph Wu, MD … |
Scope (blog) |
Current “humanized” mice not good models for studying stem cell transplants, say researchers
Scope (blog) These “humanized” mice have been useful models in some situations, such as the study of the human immune response to HIV infection or the transplantation of certain types of tissue. But recent research by cardiologist and stem cell expert Joseph Wu, MD … |