Muscular dystrophy in dogs reversed with gene therapy–are children next? – Genetic Literacy Project
Genetic Literacy Project |
Muscular dystrophy in dogs reversed with gene therapy–are children next?
Genetic Literacy Project Duchenne muscular dystrophy (DMD) is the most common and, sadly, the most severe form of the debilitating genetic disorder. Now researchers have used a new gene therapy technique to restore muscle strength and stabilize the symptoms of the disorder in … Duchenne Muscular Dystrophy Treatment Market to Partake Significant Development By 2024satPRnews (press release) |
FierceBiotech |
Chiesi dumps uniQure’s hemophilia B gene therapy
FierceBiotech Chiesi has cut its ties to uniQure’s hemophilia B gene therapy. The split gives uniQure full rights to AMT-060 but leaves it without a partner to cofund R&D as it closes in on the start of a pivotal trial. Italian drugmaker Chiesi picked up the rights … |