Gene therapy developer Orchard Therapeutics raises $110 million – Reuters
FierceBiotech |
Gene therapy developer Orchard Therapeutics raises $110 million
Reuters On Tuesday, the health agency approved Spark Therapeutics Inc’s treatment for a rare form of blindness, marking the first time the agency has approved a gene therapy for an inherited disease. ADA-SCID is an inherited disorder that damages the immune … Orchard raises $110M to bring gene therapy to marketFierceBiotech |
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CRISPR – In The Nick of Time For ALS?
ALS Research Forum But Dion and others are working on a variety of ways to reduce or eliminate expansions linked to repeat disorders using one of modern biology’s hottest tools: CRISPR-Cas gene editing. Some researchers are using the endonuclease Cas9, targeted to the … |