Tag Archives: The Stem Cell Blog

Gene therapy improves immunity in babies with ‘bubble boy’ disease – Medical Xpress

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2017-12-09 NEWS

Medical Xpress

Gene therapy improves immunity in babies with ‘bubble boy’ disease
Medical Xpress
Ewelina Mamcarz, M.D., presents research at the 2017 ASH conference that indicates that the St. Jude XSCID gene therapy has been well tolerated and effective for infants as young as 2 months old. Credit: Peter Barta / St. Jude Children’s Research

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2017-12-09 NEWS

Forbes

Excitement Builds Around Gene Therapy Cures For Hemophilia
Forbes
“The easiest thing to say is that we were absolutely blown away by them,” says K. John Pasi, of Barts Health NHS Trust and the London School of Medicine and Dentistry, who led the BioMarin study, of 9 patients. The patients all stopped using clotting
A 2nd Gene Therapy Breakthrough Against HemophiliaWebMD
First Successful Gene Therapy for Hemophilia AMedPage Today
BioMarin’s gene therapy reduces bleeding in hemophilia patientsSTAT
BioPharma Dive –Healio –Markets Insider
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2017-12-09 NEWS

New Haven Register

Yale doctor creates new weapons to kill cancer
New Haven Register
“When you use the DNA approach, that DNA gets incorporated into your genome, whereas the RNA doesn’t change your genome at all,” Katz said. “It has some safety considerations.” There are several other advantages of using RNA, Katz said. It takes far

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