FDA Clears IND Application for GALGT2 Gene Therapy for Duchenne Muscular Dystrophy – Muscular Dystrophy News
Muscular Dystrophy News |
FDA Clears IND Application for GALGT2 Gene Therapy for Duchenne Muscular Dystrophy
Muscular Dystrophy News The U.S. Food and Drug Administration (FDA) recently cleared an investigational new drug (IND) application for the GALGT2 gene therapy program for Duchenne muscular dystrophy (DMD) filed by Sarepta Therapeutics and Nationwide Children’s Hospital. Sarepta Therapeutics (SRPT): FDA Clears GALGT2 Gene Therapy Program – William BlairStreetInsider.com Sarepta Therapeutics and Nationwide Children’s Hospital Announce FDA Clearance of IND for Micro-Dystrophin Gene …Markets Insider Sarepta Therapeutics And Nationwide Children’s Hospital Announce US Food And Drug Administration (FDA …Clinical Leader |
PLoS Blogs (blog) |
PLOS iGEM 2017 – sign up now open!
PLoS Blogs (blog) Inspired by Biotreks, a synthetic biology journal for high schoolers, the Realtime Peer Review Jamboree was a live online event where authors and reviewers could comment and discuss iGEM team’s submissions in real time, responding to questions and … |
Daily Mail |
Scientists ‘completely CURE’ bowel cancer in mice using a form of pioneering immunotherapy and say it could kill …
Daily Mail They report they have achieved a ‘100-percent cure rate’ in mice without any treatment-related toxic effects. A US team developed a new type of radioimmunotherapy (RIT), which combines traditional radiation treatment and immunotherapy. They believe it … Cancer Immunotherapies Market trends, Prospect, Growth trend Anaysis and ForecastsatPRnews (press release) |
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CRISPR On Your Own
GenomeWeb Scientific American’s Annie Sneed sought to determine just how easy CRISPR is for an amateur to use. She notes that the gene-editing tool, which is simpler than previous approaches for editing genes, has raised concerns that anyone could use it to cook … |
Phys.Org |
Autonomously growing synthetic DNA strands
Phys.Org Synthetic biologists and nanobiologists are re-purposing DNA, the hereditary material present in nearly all the body’s cells, as a smart and stable self-assembling material to build nanofactories, drug-delivering nanostructures and molecular devices … |