FDA Gives Designations to Hemophilia Gene Therapies – Pharmacy Practice News
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FDA Gives Designations to Hemophilia Gene Therapies
Pharmacy Practice News Within the past week, the FDA has awarded special designations to two new gene therapy candidates for hemophilia. On Oct. 25, the FDA granted orphan drug designation and investigational new drug (IND) status to an investigational factor VIII (FVIII … With ‘breakthrough’ status and a handy nickname, BioMarin plots …Endpoints News BioMarin’s Gene Therapy for Hemophilia A Continues to ImpressRare Disease Report (blog) Breakthrough status for BioMarin ratchets up haemophilia A …pharmaphorum Healio all 7 news articles » |
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Stem cell therapy combats a one-in-a-million immune disorder for 4-year-old boy
Medical Xpress Now, thanks to chemotherapy and a new stem cell treatment, Jovon is on the mend, his mother Brittany Fluellen said. Jovon’s year-long journey started last September, when his mother first noticed he was coughing and feeling tired. She took him to the … |