Adelaide toddler’s only hope — $850000 gene therapy – The Advertiser
The Advertiser |
Adelaide toddler's only hope — $850000 gene therapy
The Advertiser The only known treatment for her condition depends on a unique gene therapy trial due to start in the next 12-18 months in Philadelphia. It follows the success of a similar trial in children with mutations of the RPE65 gene using a one-off treatment … |
