Baby gene therapy study offers hope for fatal muscle disease – ABC News
Newsweek |
Baby gene therapy study offers hope for fatal muscle disease
ABC News A first attempt at gene therapy for a disease that leaves babies unable to move, swallow and, eventually, breathe has extended the tots' lives, and some began to roll over, sit and stand on their own, researchers reported Wednesday. Only 15 babies with … Gene Therapy, New Drug Battle a Rare But Deadly Disease in Kids The Most Expensive Drug in the World Is About to Be Made Worthless by Gene Therapy New gene-replacement therapy shows promise for kids with neuromuscular disease |
