Baby gene therapy study offers hope for fatal muscle disease – Chicago Tribune
Chicago Tribune |
Baby gene therapy study offers hope for fatal muscle disease
Chicago Tribune Dr. Jerry Mendell of the Center for Gene Therapy at Nationwide Children's Hospital in Columbus, Ohio, on led a small study of gene therapy in babies born with a usually fatal neuromuscular disease. The study reported Nov. 1, 2017, that the experiment … Gene Therapy, New Drug Battle a Rare But Deadly Disease in Kids The Most Expensive Drug in the World Is About to Be Made Worthless by Gene Therapy Phase 1 study shows encouraging data for gene replacement therapy for SMA type I |
