Bluebird’s gene therapy shows promise in keeping lethal Lorenzo’s Oil disease in check – Endpoints News
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Bluebird's gene therapy shows promise in keeping lethal Lorenzo's Oil disease in check
Endpoints News After an average of 29 months following a one-time gene therapy infusion, a clear majority of boys suffering from lethal cases of cerebral adrenoleukodystrophy were alive and free of major complications from the disease — the primary endpoint in the … |
