British Biotech’s Gene Therapy for Rare ‘Bubble Baby’ Disease gets Fast-Tracked by the FDA – Labiotech.eu (blog)
Labiotech.eu (blog) |
British Biotech's Gene Therapy for Rare 'Bubble Baby' Disease gets Fast-Tracked by the FDA
Labiotech.eu (blog) Orchard Therapeutics has received rare pediatric disease designation for OTL-101, a gene therapy for the treatment of the rare disease ADA-SCID. Orchard Therapeutics, launched just a year ago in London, is developing what could be a new version of … OTL-101 granted Rare Pediatric Disease designation |
