pharmaphorumGene therapy trials held back by fragmented EU rulespharmaphorumBiotech and pharma organisations are calling for EU countries to harmonise regulations, or otherwise face falling behind in cutting-edge gene and cell therapy trials. The Europ… Continue reading
pharmaphorumGene therapy trials held back by fragmented EU rulespharmaphorumBiotech and pharma organisations are calling for EU countries to harmonise regulations, or otherwise face falling behind in cutting-edge gene and cell therapy trials. The Europ… Continue reading
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Gene therapy treatment can reach $500K for certain diseases
Genetic Literacy Project The idea behind gene therapy is that genetic material is used as a “living drug” to treat disease. Scientists have been trying to get gene therapies to work for decades, so Kymriah’s approval is historic. But the therapy’s $475,000 price tag was … |
Labiotech.eu (blog) |
French Gene Therapy for Wilson’s Disease gets Orphan Status
Labiotech.eu (blog) Vivet Therapeutics has been granted Orphan Drug Designation for its gene therapy for Wilson’s disease, VTX-801, by both the FDA and the European Commission. The French biotech Vivet Therapeutics is developing what could eventually become the first … |