Endpoints NewsBioMarin lays out its PhIII strategy for its closely-watched gene therapy for hemophilia AEndpoints NewsWhen it comes to gene therapy studies, anything other than a perfect score always raises a red flag about their future in late-stage t… Continue reading
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Quintara Biosciences Partners with Twist Bioscience to Launch New Gene Fragment and Cloning Services, qBlocks …
PR Newswire (press release) “Gene Fragments are becoming increasingly powerful in synthetic biology research, including the development of novel metabolic pathways for metabolic engineering, building variants library for protein and antibody engineering, assembling CRISPR … |
Raddington Report (blog) |
CRISPR: Close but No Cigar
Raddington Report (blog) A couple of papers were published in Nature, presenting a new system, dubbed ‘CRISPR-Cas9′, and scientists have been extolling its virtues for the past few years. CRISPR, or “Clustered Regularly Interspaced Short Palindromic Repeats” is originally a … Improving Genome Editing: CRISPR Cpf1 mechanism visualizedTechnology Networks |
STAT |
Gene therapy in hemophilia advances with big drops in patient bleeding rates
STAT t’s still early days for efforts to develop gene therapies against hemophilia, but a handful of patients treated with these one-time, potentially curative treatments have now been followed long enough to start measuring clinically relevant outcomes … BioMarin lays out its PhIII strategy for its closely-watched gene therapy for hemophilia AEndpoints News BioMarin’s gene therapy candidate for hemophilia A shows durable treatment effect in mid-stage studySeeking Alpha |
Texas Public Radio |
Oral Immunotherapy Gains Traction As An Emerging Treatment For Food Allergies
Texas Public Radio Since oral immunotherapy uses food as treatment, it’s not a therapy that has earned FDA approval. It’s simply a protocol using the allergic trigger. Silvers emphasized no one should not try this on thjeir own. OIT should be performed under the clinical … |
Texas Public Radio |
Oral Immunotherapy Gains Traction As An Emerging Treatment For Food Allergies
Texas Public Radio Since oral immunotherapy uses food as treatment, it’s not a therapy that has earned FDA approval. It’s simply a protocol using the allergic trigger. Silvers emphasized no one should not try this on thjeir own. OIT should be performed under the clinical … |
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Un nouveau type de ciseaux moléculaires pour améliorer CRISPR
Gènéthique Dans une étude publiée dans Nature, des scientifiques ont révélé la structure et l’action d’un nouveau type de « ciseaux moléculaires », connus sous le nom de Cpf1, un ARN guide endonucléasique, ce qui peut améliorer l’édition du génome CRISPR. |