Once bed ridden, Houston woman with new lease on life joins fight to make stem cell therapy available in the US – KTRK-TV
KTRK-TV |
Once bed ridden, Houston woman with new lease on life joins fight to make stem cell therapy available in the US
KTRK-TV The United States Food and Drug Administration regulates the Celltex lab in Houston where Dr. Jones can culture a patient’s stem cells. To perform the actual transfusion therapy, Sarah Hughes had to travel to Mexico, a country that has approved Celltex … |
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FDA Awards Fast-track Status to Sangamo’s Investigational Gene Therapy SB-525 for Hemophila A
Hemophilia News Today The U.S. Food and Drug Administration (FDA) has granted fast-track status to SB-525, a clinical gene therapy for hemophilia A developed by Sangamo Therapeutics in partnership with Pfizer. SB-525 delivers a human factor VIII cDNA construct and synthetic … |
ALS Research Forum |
A New Potential ALS Gene Therapy Delivers A Key Milestone
ALS Research Forum One approach, which involves gene therapy, suppresses expression of the SOD1 gene through RNA silencing-based mechanisms. This strategy, according to a 2016 study led by University of Massachusetts Medical School’s Christian Mueller, can extend the … |