OncLiveCAR T-Cell Therapy Starts to Enter MCL SpaceOncLiveWhat are the main challenges that exist for this patient population? Once ibrutinib stops working or if patients come off ibrutinib, we know that the disease may progress rapidly. These patients… Continue reading
Science DailyNew cell therapy aids heart recovery — without implanting cellsScience DailyResearchers have turned their focus to stem cell transplantation for cardiomyocyte replacement and recovery of heart function, but studies have shown that implant… Continue reading
The First CAR-T Therapy Is Not Living Up to ExpectationsLabiotech.eu (blog)Kymriah is currently waiting for FDA approval to extend the use of Kymriah to diffuse large B cell lymphoma in the US, as well as taking the therapy to Europe. But where Novarti… Continue reading
Rare Disease Report |
FDA Clears IND Application for New Gene Therapy
Rare Disease Report Mathew Shanley. This morning, it was announced by Ultragenyx Pharmaceutical Inc. that the U.S. Food and Drug Administration (FDA) has cleared the Investigational New Drug (IND) application for DTX401 for the treatment of glycogen storage disease type … Ultragenyx Pharma (RARE) Reports Filing, FDA Clearance of IND for DTX401, Gene Therapy for Treatment of …StreetInsider.com Ultragenyx Announces Filing and FDA Clearance of an Investigational New Drug Application for DTX401, a Gene …GlobeNewswire (press release) FDA on board with start of clinical development of UltraGenyx’s DTX401 for glycogen storage disorderSeeking Alpha |
Genetic Literacy Project |
ETC Group: ‘Extreme’ biotechnology critic campaigns against synthetic biology and other forms of ‘extreme genetic …
Genetic Literacy Project The ETC Group is an international environmental non-governmental organization (NGO) based in Canada whose stated purpose is to monitor “the impact of emerging technologies and corporate strategies on biodiversity, agriculture and human rights.” The … |