The Lincolnian OnlineKrystal Submits Investigational New Drug (IND) Application for KB103, Topical Gene Therapy Candidate for Dystrophic …NasdaqPITTSBURGH, March 27, 2018 (GLOBE NEWSWIRE) — Krystal Biotech Inc., ("Krystal") (NASDAQ:KRYS), … Continue reading
Genetic Literacy Project |
Does CRISPR cause unintended mutations? Authors of controversial study reverse their findings
Genetic Literacy Project [Editor’s note: The authors of a controversial report in Nature in May 2017 suggested that the popular CRISPR gene-editing technique could result in hundreds of unintended mutations. It was received with skepticism by scientists but anti-biotechnology … |
GlobeNewswire (press release) |
AveXis Gene Therapy Awarded SAKIGAKE Designation for Spinal Muscular Atrophy Type 1
GlobeNewswire (press release) CHICAGO, March 27, 2018 (GLOBE NEWSWIRE) — AveXis, Inc. (NASDAQ:AVXS), a clinical-stage gene therapy company developing treatments for patients suffering from rare and life-threatening neurological genetic diseases, today announced that Japan’s … |
Times of Malta |
Who should pay for million-dollar gene therapies?
Times of Malta If you were born with a rare form of blindness, there is now a treatment for you that may restore your eyesight. That’s because gene therapies became a clinical reality in 2017. Yet many people with rare diseases that could be treated in this way may … |