Gene Therapy Recovers LCA Patient Vision – MD Magazine
MD Magazine |
Gene Therapy Recovers LCA Patient Vision
MD Magazine The tested gene therapy, voretigene neparvovec (Luxturna) from Spark Therapeutics, is currently under FDA review for potential approval by January 2018. An injection therapy, it uses a genetically-modified version of a harmless virus that’s been … |
CBS Philly |
‘Cured’ Boy Beats Deadly Genetic Disease With Aid Of Stem Cell Tech
CBS Philly PHILADELPHIA (CBS) — Stem cell technology that genetically-modified skin cells, first created in Europe two years ago, has just been revealed with the patient, a little boy, now being called “Cured.” Hassan looks like the picture of health now, but … |
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Juno analysis of shuttered study offers clues for CAR–T
BioPharma Dive Early and rapid expansion of CAR T-cells in the body after infusion seem to correlate with severe brain toxicity in patients treated with the therapy. That amplification of modified T-cells, in turn, appeared partially linked to JCAR015’s variable cell … |
The Daily Republican |
Stem cell transplant is only hope for this vet’s survival
The Daily Republican Kristin Moore photoEven while facing health problems that could end her life, Crystal Rains Jennings still manages to brighten the day of those around her. A U.S. Army veteran, Jennings’ only chance at survival lies in the hope of a stem cell … |