Children with SMA1 Show Remarkable Progress on Gene Therapy – MD Magazine
MD Magazine |
Children with SMA1 Show Remarkable Progress on Gene Therapy
MD Magazine Cecilia Pessoa Gingerich. @CeciliaKPG. Researchers testing AVXS-101 gene therapy for the treatment of children with spinal muscular atrophy type 1 reported remarkable progress on the Children's Hospital of Philadelphia Infant Test of Neuromuscular … |
