CRISPR Restores Muscle Function in Mice – The Scientist
The Scientist |
CRISPR Restores Muscle Function in Mice
The Scientist ISTOCK, DRA_SCHWARTZUsing CRISPR, researchers have successfully treated congenital muscular dystrophy type 1A (MDC1A), a rare disease that can lead to severe muscle wasting and paralysis, in mice. The team was able to restore muscle function by … Sick Kids scientists repair genetic errors in mice with muscular dystrophy |
