First Gene Therapy For an Inherited Disease Could Soon Be Approved by The FDA – ScienceAlert
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First Gene Therapy For an Inherited Disease Could Soon Be Approved by The FDA
ScienceAlert By contrast, Luxturna, the Spark product, represents what is thought of as true gene therapy, in which a functional gene does the job of a defective one. About 1,000 to 2,000 people in the United States have inherited retinal diseases caused by a … |
