Gene therapy and rare diseases: “Is curing patients a sustainable business model?” – Genetic Literacy Project
Genetic Literacy Project |
Gene therapy and rare diseases: "Is curing patients a sustainable business model?"
Genetic Literacy Project Or they may not have enough of them in the first place, if the gene therapies treat exceedingly rare diseases. For instance, only a couple of dozen kids each year in the US and Europe are diagnosed with the type of “bubble boy” disease that Strimvelis … |
