Gene Therapy Biotech AveXis Targets ALS – ALS Research Forum
ALS Research Forum |
Gene Therapy Biotech AveXis Targets ALS
ALS Research Forum AveXis is currently using the gene therapy vector NAV AAV9, developed by REGENXBIO in Maryland, to deliver its experimental gene therapy for SMA into the spinal cord. The approach, which aims to increase levels of SMN, is beginning to show signs of … |
