Gene Therapy for Thalassemia Shows Promise – Northwestern University NewsCenter
Northwestern University NewsCenter |
Gene Therapy for Thalassemia Shows Promise
Northwestern University NewsCenter Beta-thalassemia is an inherited blood disorder caused by mutations in the beta globin gene that impair production of a fundamental component of hemoglobin, the substance in red blood cells that carries oxygen. Patients with the most severe form of … Gene Therapy For Beta-Thalassemia Could Eliminate Need for Transfusions Is bluebird bio One Step Closer to Its First Commercial Drug? |
