Gene therapy halts progression of cerebral adrenoleukodystrophy in clinical trial – Science Daily
Science Daily |
Gene therapy halts progression of cerebral adrenoleukodystrophy in clinical trial
Science Daily In a recent clinical trial, a gene therapy to treat cerebral adrenoleukodystrophy (CALD) — a neurodegenerative disease that typically claims young boys' lives within 10 years of diagnosis — effectively stabilized the disease's progression in 88 … Bluebird's gene therapy halts progression of 'devastating' disease cALD NEJM Publishes Interim Data from Study of Gene Therapy in Lorenzo |
