Gene therapy medication provides improvements in children with severe neuromuscular disease – News-Medical.net
News-Medical.net |
Gene therapy medication provides improvements in children with severe neuromuscular disease
News-Medical.net Spinraza®, the gene therapy medication, also provides significant improvements in cases with the next most severe form of neuromuscular disease, spinal muscular atrophy (SMA), which afflicts children from 6 to 18 months of age. That is shown by a study … |
