Gene Therapy, New Drug Battle a Rare But Deadly Disease in Kids – HealthDay
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Gene Therapy, New Drug Battle a Rare But Deadly Disease in Kids
HealthDay Two innovative new therapies for spinal muscular atrophy (SMA) type 1 have proven highly effective in clinical trials, researchers report. Babies with SMA are born without the gene that promotes production of survival motor neuron (SMN) protein … |
